Orphan drugs and rare - PowerPoint PPT Presentation


Upcoming Event on Orphan Drugs and Rare Diseases– | 14th – 15th October 2024

Join us at our MarketsandMarkets 5th Annual Orphan Drugs and Rare Diseases Conference in Germany, Europe, for a groundbreaking exploration of the recent advances in developing life-saving therapies, technologies in diagnosing, and strategies to enhance orphan drug development.\n\nEnquire Now @ https

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Rare Isotope Beams from FRIB - Facility Overview and Operations

FRIB (Facility for Rare Isotope Beams) is supported by the U.S. Department of Energy and Michigan State University. It utilizes advanced techniques for rare isotope beam formation, offering insights into nuclear physics. The facility operates with high beam power, serving various scientific experime

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Orphan Drugs and Rare Diseases – US Edition | 17th - 18th October 2024

Join us at our MarketsandMarkets Orphan Drugs and Rare Diseases Conference in Boston, USA for a groundbreaking exploration of the recent advances in developing life-saving therapies, technologies in diagnosing, and strategies to enhance orphan drug development.\n\nRegister Now @ \/\/events.marketsan

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Occupational Exposure to Hazardous Drugs: Risks and Prevention

Learn about the hazards of exposure to hazardous drugs, including potential health risks such as cancer, nausea, reproductive toxicity, and organ damage. Explore training modules, drug categories, and a list of hazardous drugs to ensure workplace safety. Discover NIOSH criteria for identifying hazar

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Overview of Drugs and Cosmetics Act, 1940

The Drugs and Cosmetics Act of 1940 was enacted to regulate the import, manufacture, distribution, and sale of drugs and cosmetics in India. The Act aims to ensure high standards of medical treatment, prevent substandard drugs, and establish advisory boards for different types of drugs. It sets out

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Concerns Over Weight Loss Drugs and Rare Eye Condition

Novo Nordisk shares remained stable on Thursday, despite a critical report from Harvard Medical School linking the company\u2019s weight loss drugs to a rare eye condition

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Sources of Crude Drugs: Plant, Animal, Marine, and Tissue Culture in Pharmacognosy

Crude drugs are natural substances obtained from plants, animals, and minerals. They are used without much processing and have therapeutic properties. Different plant parts like leaves, flowers, fruits, seeds, roots, bark, and stems yield various important drugs. Animals and minerals also serve as s

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Palak Mata Pita Yojana in Gujarat - Providing Financial Assistance to Orphan Children

The Palak Mata Pita Yojana in Gujarat provides financial assistance to orphan children aged 0-18 years. Started in 1978, the scheme aims to offer a domestic environment for orphan children, with financial assistance increasing over the years. Foster parents must meet income criteria, and specific do

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The Drugs and Magic Remedies (Objectionable Advertisements) Act, 1954 Overview

The Drugs and Magic Remedies (Objectionable Advertisements) Act of 1954 regulates the advertising of drugs and remedies claiming magical properties in India. It defines drugs and magic remedies, prohibits certain types of advertisements related to drugs, and aims to control misleading marketing prac

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Overview of Drugs and Cosmetics Act, 1940 and Its Rules 1945

The Drugs and Cosmetics Act of 1940 and its Rules of 1945 were established to regulate the import, manufacture, distribution, and sale of drugs and cosmetics in India. The Act ensures that only qualified individuals are involved in these processes and aims to prevent the entry of substandard or spur

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Overview of Anxiety Disorders and Antianxiety Drugs

Anxiety disorders are conditions characterized by excessive worry and fear that can interfere with daily life. Common types include generalized anxiety disorder, panic disorder, phobias, and OCD. Treatment options include psychotherapy and anxiolytic drugs such as benzodiazepines, 5HT1A agonists, be

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Overview of Anticestodal Drugs in Veterinary Pharmacology

Anticestodal drugs play a crucial role in combating tapeworm infections in veterinary medicine. These drugs are classified into taeniafuges and taenicides, with examples of natural and synthetic compounds highlighted. Natural compounds like pumpkin seeds and male fern are traditionally used for thei

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Overview of Central Drug Standard Control Organisation (CDSCO) in India

The Central Drug Standard Control Organisation (CDSCO) is the main regulatory body in India for pharmaceuticals, medical devices, and clinical trials. It functions under the Directorate General of Health Services, Ministry of Health and Family Welfare, Government of India. The CDSCO is responsible f

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Understanding Generic Drugs and Brand Name Medications

Generic drugs are identical copies of brand-name medications in dosage, strength, quality, and intended use. They contain the same active ingredients but are sold under their chemical name. This article explores the basic differences between generic and brand-name drugs, when generic drugs are marke

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Updates on European Training Requirements for Rare Diseases and Neuroendocrine Neoplasia Medicine

Comprehensive updates on European training requirements for rare diseases, rare adult solid cancers, and neuroendocrine neoplasia medicine. Initiatives include syllabi, competencies, and collaborations with international networks for advancements in the field.

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Overview of Antitubercular Drugs: Introduction, Classification, and Applications

Tuberculosis is a chronic granulomatous disease caused by Mycobacterium bovis in ruminants and Mycobacterium avium in dogs and pigs. These bacteria have a unique waxy appearance due to their cell wall composition, providing a shield against pharmacological compounds. Antitubercular drugs play a cruc

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Stakeholder Engagement in Rare Diseases: Key Role in Ghana

Rare diseases in Ghana present significant challenges such as lack of awareness, insufficient data, delayed diagnosis, and limited treatment options. To address these issues, collaborative efforts involving multiple stakeholders are essential. Actions are needed to enhance health education, improve

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Understanding Renal Block: Drugs, Excretion, and Treatment Essentials

Renal block plays a crucial role in drug excretion, with processes like glomerular filtration and tubular secretion affecting drug elimination. Factors like blood flow, physiochemical properties, and urine pH influence renal excretion of drugs. Competition between drugs for transporters can have ben

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Advances in Antimicrobial Drugs: Selective Toxicity and Classification

The development of antimicrobial drugs has significantly improved therapeutics by controlling infections and preventing complications. These drugs target invading microorganisms using selective toxicity, sparing host cells. Antimicrobial drugs are classified based on site, mechanism of action, and c

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Classification of Drugs Acting on Central Nervous System

The Central Nervous System (CNS) plays a crucial role in coordinating the body's functions and responses to the environment. Drugs acting on the CNS can be classified into CNS stimulants and CNS depressants. CNS stimulants include spinal, medullary, and cortical stimulants, with various direct and i

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EveryLife Foundation for Rare Diseases Introductory Webinar Overview

The EveryLife Foundation for Rare Diseases held an introductory webinar providing insights into their mission, foundation overview, staff members, board composition, and initiatives like advocating for biotechnology innovation and rare disease treatments through policy and law changes. The foundatio

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Managing for Multiple Values in Forest Conservation

Forest management for multiple values involves producing timber, providing recreation, protecting watersheds, and perpetuating rare species. Covering over 11,000 acres with a diverse ecosystem, the area includes oak woodlands, savannas, and prairies. With a shift towards conserving rare features and

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Pharmacology of Ovulation-Inducing Drugs

Understanding the mechanism of ovulation and hormonal regulation is key in classifying drugs used to induce ovulation. This lecture covers the pharmacology of different groups of drugs, their mechanisms of action, administration protocols, indications, efficacy rates, and adverse effects. Antiestrog

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DAVA Drugs Authentication & Verification Application by National Informatics Centre

The DAVA Drugs Authentication & Verification Application, developed by the National Informatics Centre of the Government of India, enables authentication, tracking, and tracing of Indian drugs at different packaging levels. Manufacturers maintain Unique Serial Numbers for primary and secondary packa

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Comprehensive Review of Drugs, Categories, and Drug Influence Evaluation

This mid-course review covers key aspects such as defining drugs, naming drug categories and subcategories, identifying drug categories for specific drugs, components of drug influence evaluation, and examinations conducted as part of the evaluation process. The content also includes identifying dru

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Introduction to Practical Pharmacognosy: Study of Medicines from Natural Sources

Pharmacognosy is the study of medicines derived from natural sources, exploring drugs from plants through the lenses of botany, chemistry, and pharmacology. This includes the classification of vegetable drugs based on taxonomic, chemical, and morphological characteristics. Understanding key points f

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Update on BSEE Program and Action Plan for Orphan Assets

Advisory updates on BSEE program focusing on bankruptcies, orphan assets, and decommissioning liabilities. Actions include contracting procedures, financial assurance coverage, and funding strategies to address wells, pipelines, and structures. Attention given to MIGO, ANGLO SUISSE, and ATP/BENNU as

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Understanding the Impact of Drugs on Pregnancy Development

This lecture covers factors influencing placental transfer, harmful effects of drugs at different developmental stages, FDA classifications of drugs, and teratogenic drugs. It explains how drugs cross the placenta, including physiochemical properties and stage of development affecting transfer. The

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The Forgotten Side of DNS: Orphan and Abandoned Records

DNS zone administration can be complex, leading to misconfigurations like orphan and abandoned records. Orphan records are former glue records no longer needed, while abandoned records have related domains but are unnecessary. This analysis extends prior research, examining 2K TLDs over 25 months to

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Challenges in Ensuring Critical Mineral Supply for Japan's Sustainable Industrial Activities

Japan faces challenges in securing critical minerals for sustainable industrial activities due to market failures in rare metals trade, lack of information symmetry in supply chains, and the small market size of rare metals. The Government of Japan implements policy measures such as overseas resourc

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Advancing Rare Disease Research and Healthcare Initiatives

This presentation highlights the objectives, thematic priorities, and actions of the RD-ACTION project funded by the European Union's Health Programme. It focuses on supporting the Orphanet database, promoting multi-stakeholder debates on rare diseases, and enhancing data sharing and healthcare path

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Addressing the Rare Word Problem in Neural Machine Translation

Thang Luong and team addressed the rare word problem in Neural Machine Translation by proposing an approach to track the origins of rare words in target sentences. They utilized unsupervised alignments and relative indices in the training data and implemented a post-processing method for test transl

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Understanding Drugs and Their Effects: A Comprehensive Exploration

This session delves into the world of drugs, highlighting the characteristics and effects of substances like cannabis, heroin, LSD, ecstasy, cocaine, and NPS. Participants engage in activities matching drug descriptions with names, followed by developing presentations on the drugs. Discussions inclu

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Understanding the Drugs and Magic Remedies Act 1954

The Drugs and Magic Remedies Act 1954 regulates the advertisement of drugs and prohibits the promotion of remedies claiming magical qualities. It defines various terms related to drugs and advertisements, while emphasizing the need for ethical and truthful advertising to protect the public. The Act

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Practical Guidelines for Designing Clinical Trials in Rare Diseases

This comprehensive content delves into the strategic planning of clinical trials for rare diseases, emphasizing the utilization of historical control data and the challenges associated with it. It discusses the significance of historical control in trial design, the evolving landscape of rare diseas

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Enhancing Word Representation for Rare Words by Xiao Wenyi

This article discusses methods for improving word representation for rare words, such as the count-based Skip-gram by Mikolov and the predict-based GloVe by Pennington. It explores the concepts of Skip-gram, GloVe, and issues faced by existing models in handling rare words.

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Overview of Pharmacognosy and Natural Products

Pharmacognosy is the study of medicinal drugs derived from natural sources, focusing on the properties and origins of crude drugs like plants and animals. The term was coined in 1815, emphasizing knowledge of drugs' physical, chemical, and biological properties. It is associated with various branche

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Understanding Date Rape Drugs: Rohypnol and GHB

Date rape drugs, often referred to as club drugs, are commonly used at dance clubs, concerts, raves, and parties. Rohypnol, also known as Roofies, is a depressant drug prescribed in Europe for sleep and pre-surgery relaxation. It is orally taken in various colored pills, such as olive green or white

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Understanding Anti-Tubercular Drugs: Mechanisms and Clinical Utility

Streptomycin, isoniazid, rifampin, and other anti-TB drugs are crucial in treating tuberculosis. Learn about first-line, second-line, and newer drugs, along with combination therapy. Explore the mechanisms and clinical applications of these drugs in combating TB infections.

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Rare & Endangered Species Trust: Protecting Namibia's Vultures and Pangolins

Rare & Endangered Species Trust in Namibia focuses on studying and supporting rare and endangered species, particularly vultures and pangolins. With a mission to find solutions to conservation challenges and maintain biodiversity, the trust highlights the history, crisis, and future prospects for th

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